Quiz Results Summary Firstly, we send our thanks to the CDKL5 caregivers who took the time to respond to our quiz. Although the sample is small, we have identified some insightful take-aways. The vast majority (97%) of CDD caregiver respondents to our quiz said they were interested in accessing gene therapy as a treatment should it become available. This is unsurprising as we know that the burden of a CDKL5 deficiency disorder diagnosis is high and has implications on quality of life for the entire family unit. We learned that most respondents had a decent understanding of basic drug development in the United States, including what they can do to advance the cause (enrolling in clinical research, participating in registries). However, it should be recognized that the majority did not accurately anticipate the length of time or financial investment it takes to bring a treatment like gene therapy to patients. This is significant because, if expectations are high, but the realities of the...